Black teen with sickle cell disease first gene therapy patient at Texas Medical Center
The only cure for sickle cell disease is a bone marrow transplant from a matched sibling; Helen Nduku didn’t have one. Sickle cell disease had a devastating effect on 17-year-old Helen Nduku’s life. The disease often landed her in the hospital, sometimes for weeks. “Imagine someone squeezing and stabbing you at the same time,” the…